Drug Development Under the Orphan Drug Act – It needs a fix!

There is a tremendous amount of frustration with the current state of rare/orphan drug development. With over 7,000 rare diseases only 344 therapies & treatments have been developed. So what have been the road blocks and what is the community currently doing to accelerate drug development.

One parent advocates’ perspective on this ongoing debate:

http://addiandcassi.com/wordpress/numbers-dont-add-up-only-344-new-drugs-approved-by-fda-for-30-million-americans-with-rare-disease-in-past-25-years/